Ethics approval

These papers are retrospective reviews and did not require ethics committee approval.

Conflict of Interest

ETR has consulted for, received honoraria from, and has research supported by Alexion Pharmaceuticals, AstraZeneca Rare Disease

MLB has received honoraria from Amgen, Bruno Farmaceutici, Calcilytix, Kyowa Kirin, UCB, grants and/or speaker for Abiogen, Alexion, Amgen, Bruno Farmaceutici, Echolight, Eli Lilly, Kyowa Kirin, SPA, Theramex, UCB, Consultant for Aboca, Alexion, Amolyt, Bruno Farmaceutici, Calcilytix, Kyowa Kirin, UCB

AAK has received research grants from Alexion, Amgen, Ascendis, Chugai, Radius, Takeda, Ultragenyx and is on the advisory board for Amgen, Amolyt and Takeda

SB has received advisory board participation from Alexion

KMD has received research grants and honoraria from Alexion

CD serves as an investigator, consultant, and speaker for Amgen; investigator for Radius; speaker for Alexion

SWI has received grant funding, ad hoc advisory board participation from Alexion Pharmaceuticals

MKJ has received honoria and grants from UCB, Amgen, Kyowa Kirin, Sanofi, Besin Healthcare, Abbvie

RK is a speaker and has received research funding from Alexion, AstraZeneca Rare Disease

AL is a consultant for and has received research funding and honoraria from Alexion

MEN serves as a non-paid consultant (fee equivalent donated to 501(c)3 patient advocacy groups) for Alexion

CR has received research grants and honoraria from Alexion, Kyowa Kirin, and Regeneron

CRG is a member of the Scientific Advisory Board of the HPP Global Patient Registry sponsored by Alexion Astra-Zeneca Rare Disease. She has had received honoraria for participation on this Board and has also received honoraria for select Alexion-sponsored presentations.

LS has received honoraria and grants from Alexion, Amgen, Chiesi, KyowaKirin, Novartis, Theramex, UCB

JHS serves as an Investigator and consultant for Alexion

SRS has received honoraria from, and has research supported by Alexion Pharmaceuticals, AstraZeneca Rare Disease

LMW serves as a consultant to Alexion

EML serves as an investigator, consultant, and speaker for Amgen; investigator for Radius; speaker for Alexion

DSA, HA, KA, FA, KD, SLF, FG, GG, EH, SK, IM, FM, LY, RBP declare no conflict of interest.