Abina S.H.-B., Gaspar H.B., Blondeau J., Caccavelli L., Charrier S., Buckland K., Picard C., Six E., Himoudi N., Gilmour K., McNicol A.M., Hara H., Xu-Bayford J., Rivat C., Touzot F., Mavilio F., Lim A., Treluyer J.M., Héritier S., Lefrère F., Magalon J., Pengue-Koyi I., Honnet G., Blanche S., Sherman E.A., Male F., Berry C., Malani N., Bushman F.D., Fischer A., Thrasher A.J., Galy A., and Cavazzana M. 2015. Outcomes following gene therapy in patients with severe Wiskott-Aldrich syndrome. J. Am. Med. Assoc. 313(15): 1550–1563.